Uni-Rare is a Natural History Study of vision loss progression. It is a critical and necessary step in supporting the approval of upcoming clinical trials and future therapies. It is sponsored by the Foundation Fighting Blindness and it is a new study of ∼1500 people with one of 300+ rare genes associated with inherited retinal diseases (IRDs).
Why is this study so important for finding an USH1B treatment?
- This information is crucial for deciding if a treatment is effective and if it will ultimately progress through clinical trials and be approved by the FDA.
- Without this information, companies will not invest their time and money into discovering new treatments and funding clinical trials.
Who can enroll?
- Be at least 4 years old.
- Have a clinical diagnosis of retinal disease.
- Have a rare IRD gene with at least 1 mutation that is the cause of the retinal disease.